Sarepta Therapeutics

Sarepta Therapeutics is a biopharmaceutical company focused on developing innovative therapies for rare genetic diseases, particularly those affecting muscles like Duchenne muscular dystrophy (DMD). They use advanced techniques, including gene therapy, to address the underlying causes of these conditions. By targeting specific genetic mutations, Sarepta aims to improve muscle function and overall health for patients. The company is known for its commitment to research and has developed several promising treatments that are undergoing clinical trials, showing potential to change the lives of individuals with serious, often progressive muscle disorders.