Sarepta's Pipeline

Sarepta Therapeutics is a biopharmaceutical company focused on developing therapies for rare genetic diseases, particularly Duchenne muscular dystrophy (DMD), a severe muscle-wasting condition. Their pipeline includes innovative gene therapies and exon-skipping treatments designed to target the underlying genetic causes of DMD. This approach aims to promote muscle function and improve the quality of life for affected individuals. Sarepta's pipeline also explores therapies for other genetic disorders and aims to address unmet medical needs, showcasing a commitment to advancing personalized medicine through cutting-edge science and research.