
X chromosome gene therapy
X chromosome gene therapy involves correcting or replacing faulty genes on the X chromosome to treat certain genetic disorders, particularly those affecting males or X-linked conditions. Since males have one X chromosome and females have two, addressing gene defects on the X chromosome can restore normal function or prevent disease symptoms. This therapy often uses viral vectors to deliver healthy genetic material into cells, aiming to fix the underlying genetic issue rather than just managing symptoms. It’s a targeted approach that offers potential for more permanent treatment of genetic diseases linked to the X chromosome.