Pediatric Gene Therapy

Pediatric gene therapy is a medical treatment that aims to correct or replace faulty genes in children to treat genetic disorders. It involves delivering healthy copies of genes into a patient's cells, allowing the body to produce necessary proteins that may be missing or malfunctioning due to genetic mutations. This approach has the potential to address various conditions, such as certain inherited diseases and some types of cancer. By targeting the underlying genetic issues, gene therapy offers hope for long-term improvement in health and quality of life for affected children.