Gene Therapy for Hemophilia

Gene therapy for hemophilia involves inserting a healthy copy of the gene responsible for producing the clotting factor that people with hemophilia lack. This process aims to correct the underlying genetic problem, allowing the body to produce its own clotting factor. By delivering the healthy gene into the patient's cells, either through a modified virus or other methods, it can potentially reduce or eliminate bleeding episodes and improve quality of life. This innovative approach represents a significant advancement in treating hemophilia, moving beyond traditional treatments that focus on replacing the missing factor.