Sapropterin Dihydrochloride

Sapropterin Dihydrochloride is a medication used to help certain people with a genetic disorder called phenylketonuria (PKU). In PKU, the body cannot properly process an amino acid called phenylalanine, leading to harmful buildup. Sapropterin works by increasing the activity of an enzyme that breaks down phenylalanine, reducing its levels in the blood. This can improve diet options for some patients and help prevent complications associated with PKU. It is typically prescribed alongside a special diet and regular blood tests to manage the condition effectively.