Ivacaftor

Ivacaftor is a medication used to treat cystic fibrosis, a genetic condition affecting the lungs and digestive system. It works by enhancing the function of a specific protein called CFTR, which is faulty in people with certain cystic fibrosis mutations. By improving CFTR activity, ivacaftor helps increase the movement of chloride and water in and out of cells, reducing mucus buildup and improving lung function. This can lead to better breathing, fewer infections, and improved quality of life for those with eligible mutations. It is often prescribed alongside other therapies tailored to the patient's genetic profile.