In gene therapy applications

Gene therapy is a medical technique that treats or prevents disease by directly modifying a person’s genes. It involves introducing, removing, or altering DNA within a patient's cells to correct genetic defects or enhance normal function. This can be done using viruses as delivery vehicles or other methods to target specific cells. The goal is to correct the underlying genetic cause of a condition, potentially offering a long-term or permanent solution. Gene therapy holds promise for treating genetic disorders, some cancers, and other complex diseases, improving health outcomes by addressing issues at their genetic root.