gene therapy clinical trials

Gene therapy clinical trials test new treatments that aim to correct or replace faulty genes causing disease. Researchers introduce healthy genes into patients’ cells, often using viruses as delivery vehicles, to restore normal function or halt disease progression. These trials assess safety, effectiveness, and optimal methods, involving carefully monitored steps with volunteers. The goal is to develop therapies that can provide long-term benefits, potentially curing conditions previously deemed untreatable. Participation is voluntary, with detailed informed consent ensuring patients understand potential risks and benefits.