Gene Replacement Therapy

Gene replacement therapy is a medical technique that aims to treat genetic disorders by inserting healthy copies of a gene into a person’s cells. When a faulty gene causes disease, this therapy provides a functioning version to restore normal biological processes. The new gene is usually delivered using a safe vehicle called a vector, often a modified virus. This approach can help reduce or eliminate symptoms, potentially offering a long-term or permanent solution, especially for inherited conditions. It represents a promising area of personalized medicine, targeting the root cause of genetic diseases.