Clinical Gene Therapy

Clinical gene therapy is a medical approach that treats or prevents diseases by modifying a person’s genes. It involves delivering healthy, functional copies of genes or editing existing genes to correct mutations that cause illness. This is typically done using vectors like harmless viruses to carry genetic material into the body’s cells. Gene therapy aims to address the root cause of genetic disorders, offering potential cures for conditions previously considered untreatable. It is carefully tested through clinical trials to ensure safety and effectiveness before becoming widely available.