Cerdelga

Cerdelga (the generic name is eliglustat) is a medication used to treat Gaucher disease type 1, a genetic disorder where certain fats accumulate in the body’s organs, causing symptoms like enlarged liver and spleen, bone pain, and fatigue. Cerdelga works by blocking an enzyme involved in fat production, reducing the buildup of these fats. It is taken orally as a tablet, allowing most patients to avoid the need for more invasive treatments. The medication requires careful dosing and monitoring, especially in patients with certain medical conditions or on other medications.