ASO (Antisense Oligonucleotide)

Antisense Oligonucleotides (ASOs) are short, synthetic strands of nucleic acids designed to bind specifically to the RNA messages within cells that instruct proteins to be made. By attaching to these RNA sequences, ASOs can block or alter the production of particular proteins, often those involved in disease processes. This targeted approach allows for precise modulation of gene expression, making ASOs valuable in treating genetic disorders, some cancers, and viral infections. They are usually administered as medicines and represent a promising strategy for personalized and effective therapies.