Amicus Therapeutics

Amicus Therapeutics is a biotechnology company that develops treatments for rare genetic disorders, known as lysosomal storage diseases. These are complex conditions where harmful substances build up inside cells due to enzyme deficiencies. Amicus focuses on creating innovative medicines, including enzyme replacement therapies and small molecules, to address these diseases. Their goal is to improve the quality of life for affected individuals by providing targeted, effective treatments. With advanced research and collaborations, Amicus aims to bring hope and better health outcomes to patients with previously limited options.