Adeno-Associated Viral Vectors

Adeno-associated viral (AAV) vectors are tools used in gene therapy to deliver genetic material into human cells. They are derived from a harmless virus that naturally infects humans without causing illness. Scientists modify this virus by replacing its harmful parts with therapeutic genes. When injected into the body, AAV vectors can efficiently enter specific cells and introduce new genetic instructions, potentially correcting genetic disorders or treating diseases. Because they are low in toxicity and tend to cause minimal immune response, AAV vectors are a promising and safe method for delivering targeted genetic treatments.