AAV9

AAV9, or Adeno-Associated Virus 9, is a tiny virus used in gene therapy to deliver genetic material into cells. Scientists engineer it to carry specific genes that can help treat certain genetic disorders by replacing or repairing faulty genes. AAV9 is particularly effective at reaching tissues like the brain, muscles, and heart, thanks to its ability to cross biological barriers like the blood-brain barrier. Because it doesn't cause disease itself and triggers a mild immune response, it is considered a safe and efficient vehicle for gene delivery in medical treatments.