AAV-based vectors

AAV-based vectors use a harmless virus called adeno-associated virus (AAV) to deliver genetic material into human cells. Scientists modify the virus so it cannot cause disease but can carry specific genes needed to treat or prevent diseases. Once the modified AAV enters a cell, it delivers the therapeutic gene, which the cell can then use to produce necessary proteins. This method offers a precise and relatively safe way to correct genetic disorders, and because AAVs typically don't cause strong immune reactions, they are a popular choice for gene therapy.